Use of antisense oligonucleotides to treat rare diseases By Rosie Davies   A rare disease is a disorder that affects less than 5 in 10,000 of the general population. Although individually rare, as a whole, there are up to 8000 known rare diseases, affecting approximately 3.5 million people in the UKand impacts tens of millions of individuals globally. Moreover, the number of newly published rare diseases is increasing at a